On May 20, 2025, the World Health Organization (WHO) announced that world leaders pledged at least an additional…
On May 19, 2025, Prime Medicine announced positive initial data from the first patient dosed in its ongoing…
On May 15, 2025, a team at Children’s Hospital of Philadelphia (CHOP) and Penn Medicine announced that a…
On Apr. 1, 2025, layoff notices began arriving for thousands of employees of the sprawling U.S. Department of…
On Mar. 28, 2025, the U.S. Food and Drug Administration (FDA) announced approval of Alnylam Pharmaceuticals Qfitlia™ (fitusiran),…
On Mar. 27, 2025, a Nature survey of more than 1,200 scientists, three-quarters of the total respondents are…
On Mar. 20, 2025, Alnylam Pharmaceuticals announced the U.S. Food and Drug Administration (FDA) approval of the supplemental…
On Feb. 19, 2025, scientists at St. Jude Children’s Research Hospital report results from a promising new approach…
On Jan. 14, 2025, the U.S. Food and Drug Administration’s Center for Drug Evaluation and Research (CDER) announced…
On Nov. 11, 2024, an international team of researchers has for the first time cured patients with Toxic…
On Oct. 3, 2024, scientists announced the largest whole-exome sequencing study of epilepsy to date, with more than…
On Sept. 25, 2024, a study led by scientists at Harvard Medical School announced they had developed an…
On Sept. 19, 2024, the World Health Organization (WHO) announced that Jordan had become the first country in…
On Jun. 29, 2023, the U.S. Food and Drug Administration approved Roctavian, an adeno-associated virus vector-based gene therapy…
On Apr. 26, 2021, Moderna announced that it had entered into an agreement with Sanofi for fill/finish sterile…
On Nov. 23, 2020, the U.S. Food and Drug Administration (FDA) approved Alnylam Pharmaceuticals’s Oxlumo (lumasiran) as the…
On Apr. 13, 2020, the U.S. Food and Drug Administration (FDA) announced that given the increased demand for…
On Aug. 15, 2019, the Cancer Prevention and Research Institute of Texas (CPRIT) announced that it was awarded…
On Jun. 17, 2014, Grifols opened state-of-the-art North Fractionation Facility (NFF) in Clayton, NC, where production capacity of…
ON May 16, 2012, the U.S. Senate unanimously passed a resolution (S. Res. 286) recognizing May 16, 2012,…
On Feb. 28, 2008, Rare Disease Day (also known as an “orphan” disease), was established by the European…
On Sept. 24, 2007, David H. Murdock donated $35 million to Duke University to fund the Measurement to…
In 2001, the Stephenson Cancer Center was established. Located on the University of Oklahoma (OU) Health Sciences Center…
On Oct. 25, 1996, the first gene therapy trial for patients with Hunter syndrome was begun at the…
In 1987, the U.S. Food and Drug Administration (FDA) announced revised regulations regarding Expanded Access (EA) to investigational…
On Jan. 3, 1983, the Orphan Drug Act was passed by the U.S. Congress with the leadership of…
On Jun. 5, 1981, Dr. Michael Gottlieb and colleagues of University of California at Los Angeles reported a…
In 1976, the U.S. Centers for Disease Control and Prevention (CDC) was involved in a national immunization program…
In 1963, Australian pathologist R.D.K. Reye first described this syndrome. National surveillance led to strict warnings regarding aspirin…
In 1959, Johnson ﾠ&ﾠ Johnson acquired McNeil Laboratories giving the Company a significant presence in the growing field…